Drug Discovery

D. E. Shaw Research conducts drug discovery programs both independently and in collaboration with other biopharmaceutical companies and research laboratories. All of our computational work is performed in‑house using a combination of our special‑purpose Anton supercomputers and high‑speed commodity hardware. We do not maintain in‑house “wet lab” facilities, but routinely design experiments for execution under our direction by various specialized contract research organizations (CROs).

Our drug discovery activities fall into three categories, each of which is enabled in part by the use of Anton‑based MD simulations, machine learning methods, and other advanced computational technologies:

  • Elucidating the molecular mechanisms of pathological biological processes
    • Identifying previously undiscovered biomolecular phenomena that may be relevant to the pathogenesis of potentially treatable human diseases
    • Determining how the binding of a given molecule at a given binding site modulates the function of a protein implicated in a given disease
    • Exploring at an atomic level of detail the effects of inherited or acquired mutations that are known to be associated with certain pathologies
  • Identifying new molecular strategies for pharmaceutical intervention
    • Discovering potentially druggable three‑dimensional protein configurations that have been inaccessible to experimental structure determination
    • Finding new, previously untargeted binding sites, including cryptic or ephemeral binding pockets and novel sites for allosteric modulation
    • Identifying ligand features that tend to stabilize or destabilize particular protein structures, or to promote or preclude particular interactions
  • Creating novel, precisely targeted, highly selective drugs
    • Using a combination of computational and experimental techniques to generate or screen small‑molecule compounds
    • Designing highly selective compounds that bind strongly to the target protein while avoiding toxicity‑inducing interactions with related proteins
    • Predicting and optimizing biopharmaceutical properties such as solubility and membrane permeability

Our research, technologies, and pharmaceutical expertise have each played an important role in bringing seven drugs into clinical trials. We designed three of these drugs independently; the other four were discovered under a multi‑target collaboration and licensing agreement with Relay Therapeutics (NASDAQ: RLAY), a separate company of which D. E. Shaw Research was a co‑founder. These clinical-stage drugs include:

  • Drugs we developed independently
    • DES‑9384, which inhibits TRPA1, a protein involved in such conditions as diabetic peripheral neuropathic pain, chronic lower back pain, and chronic cough
    • DES‑7987, which inhibits KCa3.1, a protein implicated in asthma, ischemic stroke, and lung fibrosis, among other diseases
  • Drugs we collaborated on with Relay Therapeutics
    • RLY‑4008, which targets the receptor tyrosine kinase FGFR2, and which was licensed by Relay to Elevar Therapeutics in 2024 as a potential therapy for cholangiocarcinoma and other solid tumors
    • RLY‑2608, which is designed to be the first allosteric, pan‑mutant (H1047X, E542X and E545X) and isoform‑selective PI3Kα inhibitor, and which is being studied as a potential treatment for breast cancer, solid tumors, and vascular malformations

D. E. Shaw Research welcomes the opportunity to collaborate with other pharmaceutical and biotech companies on the discovery and development of novel therapeutics.